@article{Yang2024, 
author = {Fei Yang and Shuqian Xu and Chao Huang and Zhiqiang Shao and Yuefen Hu and Yang Yang and Yongrong Lai and Qing Ke and Dan Liang and Yuxuan Wu},
title = {Therapeutic genome editing of an aberrant splice site in β-thalassemia by CRISPR/Cas9 with multiple sgRNAs},
year = {2024},
journal = {Genes & Diseases},
volume = {11},
number = {1},
pages = {15-18},
url = {https://www.sciopen.com/article/10.1016/j.gendis.2023.01.010},
doi = {10.1016/j.gendis.2023.01.010},
abstract = {}
}